BioSpace2dOpinion
Opinion: Companies Vie to Develop a Hunter Syndrome Therapy That Reaches the Brain
Several companies—including JCR Pharmaceuticals, Denali Therapeutics and Regenxbio— have products in the pipeline that could ...
Sinar Daily on MSN7d
PASSING ON A DESTRUCTIVE GENE
Despite having gone through this before with her first son, Yusof, and despite the doctors explaining that this was a gene ...
Hosted on MSN11mon
Rare Disease Day: Bakersfield family spreads awareness of Hunter’s syndrome
Mucopolysaccharidosis II, otherwise known has Hunter’s syndrome was detected ... With recent treatments, life expectancy has been raised to 19 years old, however– lots of children pass with ...