Only dual route gene transfer therapy in development to treat Friedreich’s ataxia with FDA IND clearance and Fast Track designation ...

Fast-track status will allow Solid Biosciences to have more frequent meetings with the FDA throughout the treatment-development process and, potentially, get the product to patients faster than would ...

For meta-analysis, 315 patients assessed based on the Scale for Assessment and Rating of Ataxia (SARA) were included. Overall, physiotherapy significantly reduced SARA scores (MD = −1.41, [95% CI: ...

Dublin, Jan. 10, 2025 (GLOBE NEWSWIRE) -- The "Friedreich Ataxia - Global Clinical Trials Review, 2024" clinical trials has been added to ResearchAndMarkets.com's offering. This report provides ...

(MENAFN- GlobeNewsWire - Nasdaq) Dublin, Jan. 10, 2025 (GLOBE NEWSWIRE) -- The "Friedreich Ataxia - Global Clinical Trials Review, 2024" clinical trials has been added to ResearchAndMarkets.com's ...

Dublin, Jan. 10, 2025 (GLOBE NEWSWIRE) -- The "Friedreich Ataxia - Global Clinical Trials Review, 2024" clinical trials has been added to ResearchAndMarkets.com's offering. This report provides top ...

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No matter how hard I fight Friedreich ataxia (FA), it keeps throwing punches, and I don’t have any gloves. Everyday tasks are becoming more difficult, and my motor skills have taken significant hits ...

for the treatment of Friedreich’s ataxia (FA). Per the company, SGT-212 is the only full-length frataxin replacement gene therapy candidate that targets the cardiac manifestations of FA.

The genesis of this program stemmed from our long term commitment to the FA community and our close relationship with the Friedreich's Ataxia Research Alliance (FARA) and members of the community ...

Solid Biosciences Inc. has gained IND clearance from the FDA for SGT-212 for the treatment of Friedreich’s ataxia (FA).