Dravet syndrome and other developmental epileptic encephalopathies are rare but devastating conditions that cause a host of symptoms in children, including seizures, intellectual disability ...

A team of researchers has developed a new gene therapy for children with Dravet syndrome, a rare type of epilepsy in children ...

Similarly, most current investigational candidates only target the symptoms. One exception is ... More than 85% of people with Dravet syndrome have an SCN1A mutation. Stoke is aiming to help ...

One such condition is Dravet syndrome (DS), which typically emerges ... and cardiac arrhythmias. These symptoms lead to premature death within the first three weeks of life. The study aimed ...

Dravet syndrome and other developmental epileptic encephalopathies are rare but devastating conditions that cause a host of symptoms in children, including seizures, intellectual disability ...

In December 2024, Praxis received Rare Pediatric Disease Designation (RPDD) from the U.S. Food and Drug Administration (FDA) ...

Phase 3 topline data from azetukalner FOS epilepsy program planned for H2 2025 in support of NDA filing and potential commercial launch– First ...

A cost-saving effort by NHS England to transition multiple sclerosis (MS) patients from Biogen Inc’s (NASDAQ:BIIB) Tysabri (natalizumab) to the biosimilar drug Tyruko has led to significant side ...

Phase 3 topline data from azetukalner FOS epilepsy program planned for H2 2025 in support of NDA filing and potential commercial launch - First of three planned Phase 3 azetukalner MDD studies underwa ...