The Health Resources and Services Administration is requesting public comments on its recommendation to add metachromatic leukodystrophy and Duchenne muscular dystrophy to the Recommended Uniform ...

DYNE-251 received FDA breakthrough therapy designation, showcasing its potential for patients with Duchenne muscular ...

A well-connected drug company and Laura Loomer wanted Kennedy ally Vinay Prasad gone. Trump Chief of Staff Susie Wiles got ...

After two patients who received the investigational CDC7 blocker died, pushing forward with SGR-2921’s development would be ...

Liquidating its stake in Arrowhead helps Sarepta cover a milestone payment and secure what one analyst described as ...

Trump loyalist Laura Loomer is openly campaigning to blunt Health and Human Services Secretary Robert F. Kennedy Jr.’s ...

A handful of drug companies have formed a group to present lawmakers with research on the negative impacts of Medicare drug ...

Sarepta Therapeutics is selling off Arrowhead Pharmaceuticals’ shares to stretch its cash runway, while also inking a share ...

The FDA’s approval of new drugs has notably slowed this year. Annual novel drug approvals averaged 52 in the first Trump Presidency and 48 under Joe Biden, but there have been only 22 in the first ...

Arrowhead PharmaceuticalsARWR stock tumbled Thursday after Sarepta TherapeuticsSRPT liquefied its entire stake in the smaller biotech company.The beleaguered biotech giant sold more than 9.2 million ...

White House chief of staff Susie Wiles intervened to save the job of a top health official President Donald Trump had fired ...

The family of a child with Duchenne are considering legal action against the health service for denying access to a drug ...